세계의 희귀질환 치료 시장 리포트(2023년)

“Rare Diseases Treatment Global Market Report 2023 ” from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on rare diseases treatment market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

Reasons to Purchase

• Gain a truly global perspective with the most comprehensive report available on this market covering 50+ geographies.
• Understand how the market has been affected by the COVID-19 and how it is responding as the impact of the virus abates.
• Assess the Russia - Ukraine war's impact on agriculture, energy and mineral commodity supply and its direct and indirect impact on the market.
• Measure the impact of high global inflation on market growth.
• Create regional and country strategies on the basis of local data and analysis.
• Identify growth segments for investment.
• Outperform competitors using forecast data and the drivers and trends shaping the market.
• Understand customers based on the latest market shares.
• Benchmark performance against key competitors.
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• Report will be updated with the latest data and delivered to you within 3-5 working days of order along with an Excel data sheet for easy data extraction and analysis.
• All data from the report will also be delivered in an excel dashboard format.

Where is the largest and fastest growing market for rare diseases treatment? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? “The rare diseases treatment market global report ” from The Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market's historic and forecast market growth by geography.

• The market characteristics section of the report defines and explains the market.
• The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
• The forecasts are made after considering the major factors currently impacting the market. These include:

The impact of sanctions, supply chain disruptions, and altered demand for goods and services due to the Russian Ukraine war, impacting various macro-economic factors and parameters in the Eastern European region and its subsequent effect on global markets.

The impact of higher inflation in many countries and the resulting spike in interest rates.

The continued but declining impact of COVID-19 on supply chains and consumption patterns.

• Market segmentations break down the market into sub markets.
• The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth. It covers the growth trajectory of COVID-19 for all regions, key developed countries and major emerging markets.
• The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
• The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.

Scope

Markets Covered:

• 1) By Drug Type: Originator Drugs (Patented Molecules); Generic Drugs

• 2) By Drug Class: Biologics; Organic Compounds

• 3) By Mode Of Administration: Injectable; Oral; Other Modes Of Administration

• 4) By Therapeutic Area: Cancer; Neurological Conditions; Cardiovascular Conditions; Musculoskeletal Conditions; Hematologic Disorders; Infectious Diseases; Metabolic Disorders; Endocrine Disorders; Other Therapeutic Areas

• 5) By Distribution Channel: Hospital Pharmacies; Specialty Pharmacies; Retail Pharmacies

• Companies Mentioned: AbbVie Inc.; Actelion Pharmaceuticals Ltd; Alexion Pharmaceuticals Inc.; Celgene Corporation; Bayer AG

• Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA

• Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa

• Time series: Five years historic and ten years forecast.

• Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,

• Data segmentations: country and regional historic and forecast data, market share of competitors, market segments.

• Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.

• Delivery format: PDF, Word and Excel Data Dashboard.

Executive Summary

Major players in the rare diseases treatment market are: AbbVie Inc., Actelion Pharmaceuticals Ltd., Alexion Pharmaceuticals Inc., Celgene Corporation, Bayer AG, Johnson & Johnson, Novartis AG, Pfizer Inc., Sanofi S.A., Eisai Co. Ltd., Merck & Co. Inc., Vertex Pharmaceuticals, Takeda Pharmaceutical Company, Eli Lilly and Company, and AstraZeneca plc.

The global rare disease treatment market is expected to grow from $149.42 billion in 2022 to $170.14 billion in 2023 at a compound annual growth rate (CAGR) of 13.87%. The Russia-Ukraine war disrupted the chances of global economic recovery from the COVID-19 pandemic, at least in the short term. The war between these two countries has led to economic sanctions on multiple countries, a surge in commodity prices, and supply chain disruptions, causing inflation across goods and services and affecting many markets across the globe. The rare disease treatment market is expected to reach $268.54 billion in 2027 at a CAGR of 12.09%.

The rare disease treatment market includes revenues earned by entities by hematology, genetic diseases, neurological diseases and oncology. The market value includes the value of related goods sold by the service provider or included within the service offering. Only goods and services traded between entities or sold to end consumers are included.

Rare diseases are diseases that impact only a small portion of the population. These diseases have a high death rate since there is little research being done on how to treat them. Rare disease treatment treats rare diseases such as genetic and metabolic diseases.

North America was the largest region in the rare disease treatment market in 2022. The regions covered in the rare disease treatment market report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa.

The main types of drugs for rare diseases treatment are originator drugs (patented molecules) and generic drugs classified as biologics and organic compounds. The originator drugs (patented molecules) are used to treat rare diseases that do not have any previous treatment. Originator drugs (patented molecules) are the first versions of a drug, patented by the founding company and are pretty expensive. The rare diseases treatments are administered through injectable, oral, and other mode of administration. The rare diseases treatments are used in cancer, neurological conditions, cardiovascular conditions, musculoskeletal conditions, hematologic disorders, infectious diseases, metabolic disorders, endocrine disorders, and other therapeutic areas. The distribution channels are hospital pharmacies, specialty pharmacies, and retail pharmacies.

The increasing burden of rare diseases is driving the rare disease treatment market. Rare diseases are diseases that affect a very small population as compared to general diseases. The increasing incidences and fatalities due to rare diseases are creating a demand for effective rare diseases treatment. For instance, according to a report published in Orphanet Journal of Rare Diseases, a UK-based open access medical journal on rare diseases, there were about 15.5 million U.S children with at least one rare. As a result, the increasing prevalence of rare diseases propels the rare disease treatment market forward.

Technological advancements are the key trends in the rare disease treatment market. Major companies in the rare disease treatment market are integrating artificial intelligence in rare disease treatment to provide a better alternative and sustain their position in the market. For instance, in August 2021, Healx, a UK-based AI-driven innovation company, launched HealNet, an AI-powered drug discovery platform for rare disease treatment. The platform is based on machine learning and artificial intelligence technology to conduct effective and fast drug discovery processes. It integrates data from multiple to form a detailed rare disease biomedical knowledge graph that is analyzed by cutting-edge AI methods.

In July 2021, AstraZeneca, a UK-based pharmaceuticals and biotechnology company, acquired Alexion Pharmaceuticals for $13.3 billion. The acquisition would enhance the presence of AstraZeneca in immunology and improve Alexion's innovative research on rare disease drugs. Alexion Pharmaceuticals is a US-based pharmaceutical company pioneering in researching treatments and drugs for patients with rare diseases.

The countries covered in the rare disease treatment market report are: Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA.

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD, unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

The rare disease treatment market research report is one of a series of new reports from The Business Research Company that provides rare disease treatment market statistics, including rare disease treatment industry global market size, regional shares, competitors with a rare disease treatment market share, detailed rare disease treatment market segments, market trends and opportunities, and any further data you may need to thrive in the rare disease treatment industry. This rare disease treatment market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future scenario of the industry.

Table of Contents

1. Executive Summary

2. Rare Diseases Treatment Market Characteristics

3. Rare Diseases Treatment Market Trends And Strategies

4. Rare Diseases Treatment Market - Macro Economic Scenario

• 4.1. COVID-19 Impact On Rare Diseases Treatment Market
• 4.2. Ukraine-Russia War Impact On Rare Diseases Treatment Market
• 4.3. Impact Of High Inflation On Rare Diseases Treatment Market

5. Rare Diseases Treatment Market Size And Growth

• 5.1. Global Rare Diseases Treatment Historic Market, 2017-2022, $ Billion
  • 5.1.1. Drivers Of The Market
  • 5.1.2. Restraints On The Market
• 5.2. Global Rare Diseases Treatment Forecast Market, 2022-2027F, 2032F, $ Billion
  • 5.2.1. Drivers Of The Market
  • 5.2.2. Restraints On the Market

6. Rare Diseases Treatment Market Segmentation

• 6.1. Global Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• Originator Drugs (Patented Molecules)
• Generic Drugs
• 6.2. Global Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• Biologics
• Organic Compounds
• 6.3. Global Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• Injectable
• Oral
• Other Modes Of Administration
• 6.4. Global Rare Diseases Treatment Market, Segmentation By Therapeutic Area, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• Cancer
• Neurological Conditions
• Cardiovascular Conditions
• Musculoskeletal Conditions
• Hematologic Disorders
• Infectious Diseases
• Metabolic Disorders
• Endocrine Disorders
• Other Therapeutic Areas
• 6.5. Global Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• Hospital Pharmacies
• Specialty Pharmacies
• Retail Pharmacies

7. Rare Diseases Treatment Market Regional And Country Analysis

• 7.1. Global Rare Diseases Treatment Market, Split By Region, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 7.2. Global Rare Diseases Treatment Market, Split By Country, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

8. Asia-Pacific Rare Diseases Treatment Market

• 8.1. Asia-Pacific Rare Diseases Treatment Market Overview
• Region Information, Impact Of COVID-19, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
• 8.2. Asia-Pacific Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 8.3. Asia-Pacific Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

9. China Rare Diseases Treatment Market

• 9.1. China Rare Diseases Treatment Market Overview
• 9.2. China Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F,$ Billion
• 9.3. China Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F,$ Billion

10. India Rare Diseases Treatment Market

• 10.1. India Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 10.2. India Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

11. Japan Rare Diseases Treatment Market

• 11.1. Japan Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 11.2. Japan Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

12. Australia Rare Diseases Treatment Market

• 12.1. Australia Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 12.2. Australia Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

13. Indonesia Rare Diseases Treatment Market

• 13.1. Indonesia Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 13.2. Indonesia Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

14. South Korea Rare Diseases Treatment Market

• 14.1. South Korea Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 14.2. South Korea Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

15. Western Europe Rare Diseases Treatment Market

• 15.1. Western Europe Rare Diseases Treatment Market Overview
• 15.2. Western Europe Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 15.3. Western Europe Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

16. UK Rare Diseases Treatment Market

• 16.1. UK Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 16.2. UK Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

17. Germany Rare Diseases Treatment Market

• 17.1. Germany Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 17.2. Germany Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

18. France Rare Diseases Treatment Market

• 18.1. France Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 18.2. France Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

19. Eastern Europe Rare Diseases Treatment Market

• 19.1. Eastern Europe Rare Diseases Treatment Market Overview
• 19.2. Eastern Europe Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 19.3. Eastern Europe Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

20. Russia Rare Diseases Treatment Market

• 20.1. Russia Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 20.2. Russia Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

21. North America Rare Diseases Treatment Market

• 21.1. North America Rare Diseases Treatment Market Overview
• 21.2. North America Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 21.3. North America Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

22. USA Rare Diseases Treatment Market

• 22.1. USA Rare Diseases Treatment Market Overview
• 22.2. USA Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 22.3. USA Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

23. South America Rare Diseases Treatment Market

• 23.1. South America Rare Diseases Treatment Market Overview
• 23.2. South America Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 23.3. South America Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

24. Brazil Rare Diseases Treatment Market

• 24.1. Brazil Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 24.2. Brazil Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

25. Middle East Rare Diseases Treatment Market

• 25.1. Middle East Rare Diseases Treatment Market Overview
• 25.2. Middle East Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 25.3. Middle East Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

26. Africa Rare Diseases Treatment Market

• 26.1. Africa Rare Diseases Treatment Market Overview
• 26.2. Africa Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion
• 26.3. Africa Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2017-2022, 2022-2027F, 2032F, $ Billion

27. Rare Diseases Treatment Market Competitive Landscape And Company Profiles

• 27.1. Rare Diseases Treatment Market Competitive Landscape
• 27.2. Rare Diseases Treatment Market Company Profiles
  • 27.2.1. AbbVie Inc.
    • 27.2.1.1. Overview
    • 27.2.1.2. Products and Services
    • 27.2.1.3. Strategy
    • 27.2.1.4. Financial Performance
  • 27.2.2. Actelion Pharmaceuticals Ltd
    • 27.2.2.1. Overview
    • 27.2.2.2. Products and Services
    • 27.2.2.3. Strategy
    • 27.2.2.4. Financial Performance
  • 27.2.3. Alexion Pharmaceuticals Inc.
    • 27.2.3.1. Overview
    • 27.2.3.2. Products and Services
    • 27.2.3.3. Strategy
    • 27.2.3.4. Financial Performance
  • 27.2.4. Celgene Corporation
    • 27.2.4.1. Overview
    • 27.2.4.2. Products and Services
    • 27.2.4.3. Strategy
    • 27.2.4.4. Financial Performance
  • 27.2.5. Bayer AG
    • 27.2.5.1. Overview
    • 27.2.5.2. Products and Services
    • 27.2.5.3. Strategy
    • 27.2.5.4. Financial Performance

28. Key Mergers And Acquisitions In The Rare Diseases Treatment Market

29. Rare Diseases Treatment Market Future Outlook and Potential Analysis

30. Appendix

• 30.1. Abbreviations
• 30.2. Currencies
• 30.3. Historic And Forecast Inflation Rates
• 30.4. Research Inquiries
• 30.5. The Business Research Company
• 30.6. Copyright And Disclaimer