니만피크병 C형 치료 시장 보고서(2025년)

Niemann-Pick disease type C (NPC) treatment refers to the medical strategies used to manage and slow the progression of Niemann-Pick disease type C, a rare inherited neurodegenerative disorder that impairs the body's ability to metabolize cholesterol and other lipids within cells. Treatment typically involves pharmacological and supportive therapies aimed at reducing neurological symptoms, stabilizing the disease, and improving the quality of life for affected individuals.

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report's Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

The main types of Niemann-Pick disease type C treatment focus on Niemann-Pick disease type C1 and Niemann-Pick disease type C2. Niemann-Pick disease type C1 (NPC1) is a rare, progressive, and fatal lysosomal storage disorder caused by mutations in the NPC1 gene. This leads to impaired cholesterol trafficking within cells, resulting in the accumulation of lipids in lysosomes, and causing severe neurological deterioration such as cognitive decline, motor dysfunction, and organ damage. NPC treatment spans various age groups, including infantile, juvenile, and adult populations, with end-users including hospitals, specialty clinics, and research and academic institutions.

The niemann-Pick disease type C treatment market research report is one of a series of new reports from The Business Research Company that provides niemann-Pick disease type C treatment market statistics, including niemann-Pick disease type C treatment industry global market size, regional shares, competitors with a niemann-Pick disease type C treatment market share, detailed niemann-Pick disease type C treatment market segments, market trends and opportunities, and any further data you may need to thrive in the niemann-Pick disease type C treatment industry. This niemann-Pick disease type C treatment market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future scenario of the industry.

The niemann-Pick disease type C treatment market size has grown strongly in recent years. It will grow from $2.68 billion in 2024 to $2.93 billion in 2025 at a compound annual growth rate (CAGR) of 9.2%. The growth observed during the historic period can be attributed to the expansion of healthcare infrastructure, a rising number of cases involving mutations in the NPC1 and NPC2 genes, a growing prevalence of Niemann-Pick disease, increased government funding for research into rare disease treatments, and heightened awareness and advocacy efforts.

The niemann-Pick disease type C treatment market size is expected to see strong growth in the next few years. It will grow to $4.14 billion in 2029 at a compound annual growth rate (CAGR) of 9.1%. The growth projected during the forecast period can be attributed to increasing research and development activities, a growing number of pipeline drugs, a high prevalence of rare diseases, the emerging popularity of gene therapy, and significant advancements in genetic therapies. Key trends during this period include advancements in technology, the rise of personalized medicine for lysosomal storage disorders, progress in genetic and molecular research, breakthroughs in biotechnology, and the development of innovative therapeutics.

The growing prevalence of Alzheimer's disease is expected to accelerate the expansion of the Niemann-Pick disease type C (NPC) treatments market. Alzheimer's disease is a progressive neurodegenerative disorder characterized by the buildup of beta-amyloid plaques and tau protein tangles in the brain, leading to cognitive decline, memory loss, and difficulties with daily functioning, ultimately resulting in severe dementia and neurodegeneration. The increasing prevalence of Alzheimer's disease is largely due to the aging global population. As life expectancy increases, especially in developed nations, the risk of age-related diseases such as Alzheimer's also rises, since advancing age is the most significant known risk factor for the condition. NPC treatment contributes to Alzheimer's disease research by offering insights into lysosomal storage disorders and dysfunctions in lipid metabolism. For example, in May 2024, the Alzheimer's Society, a UK-based health organization, estimated that 982,000 people in the UK were living with dementia in 2024, with more than a third undiagnosed. This number is expected to reach 1.4 million by 2040. Therefore, the growing prevalence of Alzheimer's disease is driving the growth of the Niemann-Pick disease type C treatments market.

Leading companies in the Niemann-Pick disease type C (NPC) treatment market are focusing on developing innovative therapies, such as neuroprotective treatments, aimed at slowing disease progression and improving patient outcomes. Neuroprotective therapies are designed to protect the brain and nervous system from damage or degeneration, with the goal of preserving neurological function in conditions such as neurodegenerative diseases. For example, in September 2024, IntraBio Inc., a US-based biopharmaceutical company, received approval from the United States Food and Drug Administration (FDA) for AQNEURSA (levacetylleucine), the first stand-alone therapy for Niemann-Pick Disease Type C (NPC). This approval followed promising Phase III trial results, showing significant neurological improvements in NPC patients within 12 weeks. AQNEURSA offers a long-awaited treatment option for individuals suffering from this rare lysosomal storage disorder, which affects movement, cognition, and daily function. IntraBio also intends to explore AQNEURSA's potential in treating other neurodegenerative and neurodevelopmental disorders.

In December 2023, Cyclo Therapeutics, Inc., a US-based biotechnology firm, merged with Applied Molecular Transport Inc. for $10.2 million. This merger is aimed at strengthening Cyclo Therapeutics' financial and strategic position by utilizing additional resources, extending its financial runway, and advancing the clinical development and regulatory approval process for Trappsol Cyclo, a potential treatment for Niemann-Pick Disease Type C1 (NPC1). This treatment will undergo the pivotal Phase 3 global study (TransportNPC). Applied Molecular Transport Inc. is a US-based clinical-stage biopharmaceutical company.

Major players in the niemann-pick disease type c treatment market are Merck & Co. Inc., Mayo Clinic, Boston Children's Hospital, Cincinnati Children's Hospital Medical Center, Mallinckrodt Pharmaceuticals, Myriad Genetics Inc., Rainbow Children's Hospital, CENTOGENE N.V., The Florey Institute of Neuroscience and Mental Health, Insilico Medicine Inc., National Organization for Rare Disorders (NORD), Zevra Therapeutics Inc., Azafaros A.G., IntraBio Inc., National Niemann-Pick Disease Foundation (NNPDF), Bloomsbury Genetic Therapies Ltd., CTD Holdings Inc., Okklo Life Sciences, Vtesse Inc., Cyclo Therapeutics Inc., Mandos Health.

North America was the largest region in the niemann-pick disease type C treatment market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in niemann-Pick disease type C treatment report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa.

The countries covered in the niemann-Pick disease type C treatment market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

The niemann-Pick disease type C treatment market includes revenues earned by entities through medication management, symptom management, neurological care, liver care, and genetic counseling. The market value includes the value of related goods sold by the service provider or included within the service offering. Only goods and services traded between entities or sold to end consumers are included.

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD, unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

Niemann-Pick Disease Type C Treatment Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on niemann-pick disease type c treatment market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

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Where is the largest and fastest growing market for niemann-pick disease type c treatment ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? The niemann-pick disease type c treatment market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market's historic and forecast market growth by geography.

• The market characteristics section of the report defines and explains the market.
• The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
• The forecasts are made after considering the major factors currently impacting the market. These include:

The forecasts are made after considering the major factors currently impacting the market. These include the Russia-Ukraine war, rising inflation, higher interest rates, and the legacy of the COVID-19 pandemic.

• Market segmentations break down the market into sub markets.
• The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth. It covers the growth trajectory of COVID-19 for all regions, key developed countries and major emerging markets.
• The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
• The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.

Scope

• Markets Covered:1) By Disease Type: Niemann-Pick Diseases Type C1; Niemann-Pick Diseases Type C2
• 2) By Age Group: Infantile; Juvenile; Adult
• 3) By End-User: Hospitals; Specialty Clinics; Research And Academic Institutes
• Subsegments:
• 1) By Niemann-Pick Disease Type C1: Pharmacological Treatment; Gene Therapy; Substrate Reduction Therapy; Supportive Care
• 2) By Niemann-Pick Disease Type C2: Enzyme Replacement Therapy; Pharmacological Treatment; Gene Therapy; Supportive Care
• Companies Mentioned: Merck & Co. Inc.; Mayo Clinic; Boston Children's Hospital; Cincinnati Children's Hospital Medical Center; Mallinckrodt Pharmaceuticals
• Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA; Canada; Italy; Spain
• Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa
• Time series: Five years historic and ten years forecast.
• Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,
• Data segmentations: country and regional historic and forecast data, market share of competitors, market segments.
• Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.
• Delivery Format: PDF, Word and Excel Data Dashboard.

Table of Contents

1. Executive Summary

2. Niemann-Pick Disease Type C Treatment Market Characteristics

3. Niemann-Pick Disease Type C Treatment Market Trends And Strategies

4. Niemann-Pick Disease Type C Treatment Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

5. Global Niemann-Pick Disease Type C Treatment Growth Analysis And Strategic Analysis Framework

• 5.1. Global Niemann-Pick Disease Type C Treatment PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)
• 5.2. Analysis Of End Use Industries
• 5.3. Global Niemann-Pick Disease Type C Treatment Market Growth Rate Analysis
• 5.4. Global Niemann-Pick Disease Type C Treatment Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)
• 5.5. Global Niemann-Pick Disease Type C Treatment Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)
• 5.6. Global Niemann-Pick Disease Type C Treatment Total Addressable Market (TAM)

6. Niemann-Pick Disease Type C Treatment Market Segmentation

• 6.1. Global Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Niemann-Pick Diseases Type C1
• Niemann-Pick Diseases Type C2
• 6.2. Global Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Infantile
• Juvenile
• Adult
• 6.3. Global Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Hospitals
• Specialty Clinics
• Research And Academic Institutes
• 6.4. Global Niemann-Pick Disease Type C Treatment Market, Sub-Segmentation Of Niemann-Pick Diseases Type C1, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Pharmacological Treatment
• Gene Therapy
• Substrate Reduction Therapy
• Supportive Care
• 6.5. Global Niemann-Pick Disease Type C Treatment Market, Sub-Segmentation Of Niemann-Pick Diseases Type C2, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Enzyme Replacement Therapy
• Pharmacological Treatment
• Gene Therapy
• Supportive Care

7. Niemann-Pick Disease Type C Treatment Market Regional And Country Analysis

• 7.1. Global Niemann-Pick Disease Type C Treatment Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 7.2. Global Niemann-Pick Disease Type C Treatment Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8. Asia-Pacific Niemann-Pick Disease Type C Treatment Market

• 8.1. Asia-Pacific Niemann-Pick Disease Type C Treatment Market Overview
• Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
• 8.2. Asia-Pacific Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 8.3. Asia-Pacific Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 8.4. Asia-Pacific Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

9. China Niemann-Pick Disease Type C Treatment Market

• 9.1. China Niemann-Pick Disease Type C Treatment Market Overview
• 9.2. China Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
• 9.3. China Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
• 9.4. China Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

10. India Niemann-Pick Disease Type C Treatment Market

• 10.1. India Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 10.2. India Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 10.3. India Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11. Japan Niemann-Pick Disease Type C Treatment Market

• 11.1. Japan Niemann-Pick Disease Type C Treatment Market Overview
• 11.2. Japan Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 11.3. Japan Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 11.4. Japan Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12. Australia Niemann-Pick Disease Type C Treatment Market

• 12.1. Australia Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 12.2. Australia Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 12.3. Australia Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13. Indonesia Niemann-Pick Disease Type C Treatment Market

• 13.1. Indonesia Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 13.2. Indonesia Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 13.3. Indonesia Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14. South Korea Niemann-Pick Disease Type C Treatment Market

• 14.1. South Korea Niemann-Pick Disease Type C Treatment Market Overview
• 14.2. South Korea Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 14.3. South Korea Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 14.4. South Korea Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15. Western Europe Niemann-Pick Disease Type C Treatment Market

• 15.1. Western Europe Niemann-Pick Disease Type C Treatment Market Overview
• 15.2. Western Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 15.3. Western Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 15.4. Western Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16. UK Niemann-Pick Disease Type C Treatment Market

• 16.1. UK Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 16.2. UK Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 16.3. UK Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17. Germany Niemann-Pick Disease Type C Treatment Market

• 17.1. Germany Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 17.2. Germany Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 17.3. Germany Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18. France Niemann-Pick Disease Type C Treatment Market

• 18.1. France Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 18.2. France Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 18.3. France Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19. Italy Niemann-Pick Disease Type C Treatment Market

• 19.1. Italy Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 19.2. Italy Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 19.3. Italy Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20. Spain Niemann-Pick Disease Type C Treatment Market

• 20.1. Spain Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 20.2. Spain Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 20.3. Spain Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21. Eastern Europe Niemann-Pick Disease Type C Treatment Market

• 21.1. Eastern Europe Niemann-Pick Disease Type C Treatment Market Overview
• 21.2. Eastern Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 21.3. Eastern Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 21.4. Eastern Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22. Russia Niemann-Pick Disease Type C Treatment Market

• 22.1. Russia Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 22.2. Russia Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 22.3. Russia Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23. North America Niemann-Pick Disease Type C Treatment Market

• 23.1. North America Niemann-Pick Disease Type C Treatment Market Overview
• 23.2. North America Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 23.3. North America Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 23.4. North America Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24. USA Niemann-Pick Disease Type C Treatment Market

• 24.1. USA Niemann-Pick Disease Type C Treatment Market Overview
• 24.2. USA Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 24.3. USA Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 24.4. USA Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25. Canada Niemann-Pick Disease Type C Treatment Market

• 25.1. Canada Niemann-Pick Disease Type C Treatment Market Overview
• 25.2. Canada Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 25.3. Canada Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 25.4. Canada Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26. South America Niemann-Pick Disease Type C Treatment Market

• 26.1. South America Niemann-Pick Disease Type C Treatment Market Overview
• 26.2. South America Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 26.3. South America Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 26.4. South America Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27. Brazil Niemann-Pick Disease Type C Treatment Market

• 27.1. Brazil Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 27.2. Brazil Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 27.3. Brazil Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28. Middle East Niemann-Pick Disease Type C Treatment Market

• 28.1. Middle East Niemann-Pick Disease Type C Treatment Market Overview
• 28.2. Middle East Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 28.3. Middle East Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 28.4. Middle East Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29. Africa Niemann-Pick Disease Type C Treatment Market

• 29.1. Africa Niemann-Pick Disease Type C Treatment Market Overview
• 29.2. Africa Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 29.3. Africa Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 29.4. Africa Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

30. Niemann-Pick Disease Type C Treatment Market Competitive Landscape And Company Profiles

• 30.1. Niemann-Pick Disease Type C Treatment Market Competitive Landscape
• 30.2. Niemann-Pick Disease Type C Treatment Market Company Profiles
  • 30.2.1. Merck & Co. Inc. Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.2. Mayo Clinic Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.3. Boston Children's Hospital Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.4. Cincinnati Children's Hospital Medical Center Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.5. Mallinckrodt Pharmaceuticals Overview, Products and Services, Strategy and Financial Analysis

31. Niemann-Pick Disease Type C Treatment Market Other Major And Innovative Companies

• 31.1. Myriad Genetics Inc.
• 31.2. Rainbow Children's Hospital
• 31.3. CENTOGENE N.V.
• 31.4. The Florey Institute of Neuroscience and Mental Health
• 31.5. Insilico Medicine Inc.
• 31.6. National Organization for Rare Disorders (NORD)
• 31.7. Zevra Therapeutics Inc.
• 31.8. Azafaros A.G.
• 31.9. IntraBio Inc.
• 31.10. National Niemann-Pick Disease Foundation (NNPDF)
• 31.11. Bloomsbury Genetic Therapies Ltd.
• 31.12. CTD Holdings Inc.
• 31.13. Okklo Life Sciences
• 31.14. Vtesse Inc.
• 31.15. Cyclo Therapeutics Inc.

32. Global Niemann-Pick Disease Type C Treatment Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Niemann-Pick Disease Type C Treatment Market

34. Recent Developments In The Niemann-Pick Disease Type C Treatment Market

35. Niemann-Pick Disease Type C Treatment Market High Potential Countries, Segments and Strategies

• 35.1 Niemann-Pick Disease Type C Treatment Market In 2029 - Countries Offering Most New Opportunities
• 35.2 Niemann-Pick Disease Type C Treatment Market In 2029 - Segments Offering Most New Opportunities
• 35.3 Niemann-Pick Disease Type C Treatment Market In 2029 - Growth Strategies
  • 35.3.1 Market Trend Based Strategies
  • 35.3.2 Competitor Strategies

36. Appendix

• 36.1. Abbreviations
• 36.2. Currencies
• 36.3. Historic And Forecast Inflation Rates
• 36.4. Research Inquiries
• 36.5. The Business Research Company
• 36.6. Copyright And Disclaimer
• 250617_r34910_Niemann_Pick_Disease_Type_C_Treatment_GMR_2025